For Patients & Families
From your first inquiry to your last visit, our team takes the time to explain every step, coordinate around your schedule, and make sure our facility meets your accessibility needs.
What Is a Clinical Trial
Every approved therapy for neuromuscular disease began as a clinical trial. By participating, you gain access to treatments that are not yet available to the public — and you contribute to the science that will help others in the future.
Trials follow a written plan called a protocol, reviewed by an independent ethics board and overseen by regulators. Your participation is entirely voluntary. You may ask anything at any time, and you may withdraw at any point, for any reason, without affecting the care you receive elsewhere.
Share a little about yourself or your family member. A member of our team responds personally.
We explain what studies are open, what each study involves, and whether any fit your situation — in plain language.
A specialized assessment confirms eligibility. Accessibility needs are arranged before you arrive.
Visits are scheduled around your life. The same team supports you throughout, and you may withdraw at any time.
We stay in contact after the study closes and let you know about future opportunities that may fit.
Safety and Your Rights
Every study follows a protocol reviewed by an independent ethics board called an Institutional Review Board (IRB) and monitored by regulators.
You receive a full explanation of the study before agreeing to anything, and you keep a copy of everything you sign.
You may leave a study at any time, for any reason, without affecting the care you receive elsewhere.
Safety data is reviewed throughout the study, and your care team is reachable between visits if a need arises.
Registering your interest places you on our contact list so that we can inform you about relevant upcoming trials. There is no obligation, and sharing your information does not enroll you in a study.
Register your interest